Rugonersen, a potentially best-in-class antisense oligonucleotide (ASO) therapy in development for Angelman syndrome, advanced into the pivotal ...

The Angelman Syndrome Foundation (ASF) and Citizen Health today announced a partnership to bring Ari, Citizen Health's AI advocate for rare disease families, to the Angelman community. ASF is among ...

Emily Wallace’s “mom intuition” led to her son’s Angelman syndrome diagnosis at just 18 months ...

A new review sheds light on the complex molecular mechanisms behind Angelman syndrome (AS), a rare neurogenetic disorder, and explores how cutting-edge gene-targeting therapies may offer more ...

Learn what every caregiver should know about Angelman syndrome, including its symptoms, diagnosis, daily care strategies, ...

Transaction to provide Oak Hill Bio with approximately $175 million in gross proceeds, including $75 million of cash in ...

Actor Colin Farrell is launching a new foundation to raise awareness of a rare genetic condition called Angelman syndrome, so that his son and others with the disorder will have more support and ...

Frances Arnold, PhD, winner of the 2018 Nobel Prize in Chemistry, has been awarded a two-year grant by the Foundation for Angelman Syndrome Therapeutics (FAST) to develop new molecular tools that ...

Emily Wallace received backlash for a video showing her and her husband installing a barrier in the backseat of her car before a 10-hour road trip ...

In recent years, Colin Farrell has been speaking more openly about his experience of having a child with disabilities, with his eldest son, James, born with Angelman syndrome. Farrell was 27 years old ...

Babies born with a faulty maternal copy of the UBE3A gene will develop Angelman syndrome, a severe neurodevelopmental disorder with no cure and limited treatments. Now, for the first time, scientists ...