About one in every 3,500-5,000 boys worldwide is born with Duchenne Muscular Dystrophy, or DMD, a rare genetic condition that ...

Muscular dystrophy (MD) is a group of genetic diseases that cause your muscles to progressively weaken and degenerate. There are several types of MD, each with its own symptoms, but they all involve ...

Your muscles need continuous maintenance to stay strong and healthy. Duchenne muscular dystrophy (DMD) happens when there is a change in a person's genetic instructions that affects the production of ...

The first gene therapy for children with Duchenne muscular dystrophy has been approved by the U.S. Food and Drug Administration. The therapy can be used in 4- and 5-year-olds with the degenerative ...

Conserving energy is an essential component of living with Duchenne muscular dystrophy (DMD). Fatigue, both physical and mental, is extremely common with this genetic disease that causes progressive ...

Gemma Biotherapeutics ("GEMMABio"), a clinical‑stage, global, genetic medicines company, today announced the presentation of preclinical data supporting candidate declaration for GB703, a novel, ...

Regenxbio’s gene therapy for Duchenne muscular dystrophy has smashed the primary endpoint of its pivotal trial, securing a ...

The FDA has an opportunity to reset its relationship with rare disease families and help, not obstruct. The new commissioner ...

Myotonic muscular dystrophy, which is sometimes called myotonic dystrophy, is a type of muscular dystrophy. There are two types of myotonic muscular dystrophy, described as type 1 (DM 1) and type 2 ...

On June 2, teams across Major League Baseball will recognize the 5th Annual Lou Gehrig Day. June 2 was selected because it was the date Gehrig became the Yankees' starting first baseman. It is also ...

Tributes poured in for Gilbert Gottfried on Tuesday after news broke that he died in Manhattan. The 67-year-old comedian’s family shared on Twitter that he passed away “after a long illness.” ...